Список литературы
1 Guidance for Industry: Preclinical Assessment of Investigational Cellular and Gene Therapy Products; Availability
A Notice by the Food and Drug Administration on 11/25/2013 Guidance for Industry: Preclinical Assessment of Investigational Cellular and Gene Therapy Products, 2013
2 Mikheev A. A. et al. Сationic liposomes as delivery systems for nucleic acids //Fine Chemical Technologies. – 2020. – Т. 15. – №. 1. – С. 7-27.
3 Michel T. et al. Cationic nanoliposomes meet mRNA: Efficient delivery of modified mRNA using hemocompatible and stable vectors for therapeutic applications //Molecular Therapy-Nucleic Acids. – 2017. – Т. 8. – С. 459-468.
4 Liu C. et al. Barriers and strategies of cationic liposomes for cancer gene therapy //Molecular Therapy Methods & Clinical Development. – 2020. – Т. 18. – С. 751-764.
5 Waehler R., Russell S.J., Curiel D.T. Engineering targeted viral vectors for gene therapy. Nat. Rev. Genet. 2007;8:573-587. https://doi.org/10.1038/nrg2141
6 Felgner P. L. et al. Lipofection: a highly efficient, lipid-mediated DNA-transfection procedure //Proceedings of the National Academy of Sciences. – 1987. – Т. 84. – №. 21. – С. 7413-7417.
7 Sayed N. et al. Gene therapy: Comprehensive overview and therapeutic applications //Life sciences. – 2022. – Т. 294. – С. 120375.
8 Meyer O. et al. Cationic liposomes coated with polyethylene glycol as carriers for oligonucleotides //Journal of Biological Chemistry. – 1998. – Т. 273. – №. 25. – С. 15621-15627.
9 Conner S.D., Schmid S.L. Regulated portals of entry into the cell. Nature. 2003;422:37-44. https://doi.org/10.1038/nature01451
10 . Jones C.H., Chen C.-K., Ravikrishnan A., Rane S., Pfeifer B.A. Overcoming nonviral gene delivery barriers: perspective and future. Mol. Pharmaceutics. 2013;10:4082-4098. https://doi.org/10.1021/mp400467x
11 Ward C.M., Read M.L., Seymour L.W. Systemic circulation of poly(L-lysine)/DNA vectors is influenced by polycation molecular weight and type of DNA: differential circulation in mice and rats and the implications for human gene therapy. Blood. 2001;97(8):2221-2229. https://doi.org/10.1182/blood.v97.8.2221
12 Van der Aa M.A., Mastrobattista E., Oosting R.S., Hennink W.E., Koning G.A., Crommelin D.J. The nuclear pore complex: the gateway to successful nonviral gene delivery. Pharm. Res. 2006;23(3):447-459. https://doi.org/10.1007/s11095-005-9445-4
13 Богданенко Е.В., Свиридов Ю.В., Московцев А.А., Жданов Р.И. Невирусный перенос генов in vivo в генной терапии. Вопросы медицинской химии. 2000;46(3):226-245. [Bogdanenko E.V., Sviridov Yu.V., Moskovtsev A.A., Zhdanov R.I. Non-viral gene transfer in vivo in gene therapy. Voprosy meditsinskoi khimii = Issues of Medicinal Chemistry. 2000;46(3):226-245 (in Russ.).]
14 Kulkarni P.R., Yadav J.D., Vaidya K.A. Liposomes: a novel drug delivery system. Int. J. Curr. Pharm. Res. 2010;3(2):10-18.
15 Goyal P., Goyal K., Kumar S.G., Singh A., Katare O.P., Mishra D.N. Liposomal drug delivery systems – Clinical applications. Acta Pharm. 2005;55:1-25. 78. Byk T., Haddada H., Vainchenker W., Louache F. Lipofectamine and related cationic lipids strongly improve adenoviral infection efficiency of primitive human hematopoietic cells. Hum. Gene Ther. 1998;9:2493-2502. https://doi.org//10.1089/hum.1998.9.17-2493
16 Cardarelli F., Digiacomo L., Marchini C., Amici A., Salomone F., Fiume G., Rossetta A., Gratton E., Pozzi D., Caracciolo G. The intracellular trafficking mechanism of lipofectaminebased transfection reagents and its implication for gene delivery. Scientific Rep. 2016;6(25879). https://doi.org//10.1038/srep25879
17 Byk T., Haddada H., Vainchenker W., Louache F. Lipofectamine and related cationic lipids strongly improve adenoviral infection efficiency of primitive human hematopoietic cells. Hum. Gene Ther. 1998;9:2493-2502. https://doi.org//10.1089/hum.1998.9.17-2493
18 Zhao M., Yang H., Jiang X., Zhou W., Zhu B., Zeng Y., Yao K., Ren C. Lipofectamine RNAiMAX: an efficient siRNA transfection reagent in human embryonic stem cells. Mol. Biotechnol. 2008;40:19-26. https://doi.org//10.1007/s12033-008-9043-x 1
19 Zuris J.A., Thompson D.B., Shu Y., Guilinger J.P., Bessen J.L., Hu J.H., Maeder M.L., Joung J.K., Chen Z.Y., Liu D.R. Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo. Nat. Biotechnol. 2015; 33:73-80. https://doi.org//10.1038/nbt.3081